On April 28, 2026 the Jeffrey Modell Foundation (JMF) will host Luigi D. Notarangelo, M.D., the Chief of the Immune Deficiency Genetics Section at the National Institute of Allergy and Infectious ...
Upon approval, Rocket has been awarded a priority review voucher, which currently fetch around $200m on the secondary market.
Kids with severe LAD-I, caused by ITGB2 mutations, are at risk of life-threatenin ...
Researchers have revealed a novel association between chromosome 18q deletion syndrome and late-onset combined immunodeficiency (LOCID). Their finding challenges the previously held notion that 18q ...
Dr. Donald Kohn has been developing gene therapies for rare pediatric immune disorders for over 30 years. This week, his role in a clinical trial has culminated in the first-ever U.S. Food and Drug ...
Primary immunodeficiency (PI) is a group of more than 400 disorders that affect the immune system. In people with PI, the immune system is weakened or missing important components, making it harder ...
Primary immunodeficiency (PI) not only increases your risk of frequent and serious infections, but can also make you more likely to develop autoimmune diseases — conditions where the immune system ...
The influenza virus or flu is a contagious respiratory illness that can generate mild, moderate, or severe symptoms. Healthy individuals that contract the virus may feel mild symptoms, but recover ...
A study just published in the journal Microbiome, describes for the first time the intestinal microbiome and metabolome in patients with (genetically acquired) CTLA4 deficiency. CTLA4 is an immune ...
Rocket Pharmaceuticals (RCKT) stock jumps as FDA approves its gene therapy Kresladi for a rare immune disease called ...